Ex vivo modification of hematopoietic stem and progenitor cells for gene therapy.

Ex vivo modification of hematopoietic stem and progenitor cells for gene therapy. Williams DA, Kohn DB, Thrasher AJ. Mol Ther. 2025 May 7;33(5):2141-2153. doi: 10.1016/j.ymthe.2025.03.058. Epub 2025 Apr 1. PMID: 40176348 Review.